Application of ADAR in Development of Rare Disease Therapeutics

Time: 9:10 am
day: Day Two


• Why we are using RNA Editing over contemporary genome engineering technologies (CRISPR, TALENs and Zinc Fingers)
• Why is ADAR our focus and how does it solve the problems that CRISPR presented?
• Exploring ShapeTX’s technology core platform “RNAfix”